VANCOUVER — Autologous hematopoietic stem cell (HSC) gene therapy may offer a safe and effective alternative to allogeneic bone marrow transplant for patients with cerebral adrenoleukodystrophy, ...
THE GROUND BY SUNDAY AFTERNOON. ALL RIGHT. THANK YOU OLGA. ALDI IS A RARE GENETIC DISEASE THAT AFFECTS 1 IN 17,000 PEOPLE WORLDWIDE. THE DIAGNOSIS HIT ONE FAMILY WHO IS ORIGINALLY FROM ALBUQUERQUE.
Alcohol-associated liver disease (ALD) is a significant global health concern, accounting for approximately 5% of all disease and injury. In the United States, the prevalence of ALD has increased ...
A North Texas family is on a mission to save lives. Tyler and Taylor's 10-month-old son William has a genetic disorder with no cure, and while it's rare, every newborn is screened for it. Newborn ...
(MENAFN- PR Newswire) BARCELONA, Spain and DÜSSELDORF, Germany, Feb. 29, 2024 /PRNewswire/ -- Neuraxpharm Group (Neuraxpharm), a leading European specialty pharmaceutical company focused on the ...
Please provide your email address to receive an email when new articles are posted on . Most patients who received Skysona for cerebral adrenoleukodystrophy did not have major functional disabilities ...
NeuroVia Closes Series A Financing Round of $14M to Develop Novel Treatment Option for X-ALD Disease
CAMBRIDGE, Mass.--(BUSINESS WIRE)--NeuroVia, Inc., a biopharmaceutical company focused on developing innovative therapies for rare genetic neurological diseases, announced the closing of a Series A ...
GAITHERSBURG, Md., July 09, 2025 (GLOBE NEWSWIRE) -- Altimmune, Inc. (Nasdaq: ALT), a late clinical-stage biopharmaceutical company developing novel peptide-based therapeutics for liver and ...
outlet community indicate in locked contenttrend art alcohol alcohol locked contentindicate Festivals in problems locked contentalcohol Karma alcohol cases locked content in Bhutanese problems result ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results