Non-human primate study results demonstrate improvements in skeletal and cardiac muscle delivery efficacy, safety potential, human translatability, and manufacturability over prior AAV capsids ...
PARIS, France (September 12, 2024) - Genethon, the pioneering French laboratory and leader in the research and development of gene therapies for rare diseases, announced today publication in Nature ...
Gene therapy is a promising approach for the treatment of numerous diseases. Critical to its success is a safe and effective method for the delivery of genes to appropriate tissues. Accomplishing this ...
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