When Doug Ingram became Sarepta Therapeutics’ CEO in 2017, he didn’t have a connection to muscular dystrophy, but he has ...

On Midday Minute for Wednesday Sen. John Carley has been found, a South Dakotan received the Medal of Honor and a local family is looking to find a cure for ...

New York, Jan. 26, 2026 (GLOBE NEWSWIRE) -- In recognition of Rare Disease Day on February 28, the Muscular Dystrophy Association (MDA) is sharing powerful community stories throughout the month that ...

A new mouse model mimicking the liver symptoms of myotonic dystrophy type 1 -- the most prevalent form of adult-onset muscular dystrophy -- provides insight into why patients develop fatty liver ...

A new gene therapy for Duchenne muscular dystrophy (DMD) has shown promise in not only slowing the progression of the disease but potentially even reversing the muscle damage, with human trials set to ...

The MDA Shamrocks campaign returns nationwide, raising funds for neuromuscular research and families living with ALS and other rare diseases.

This award honors an emerging leader shaping the future of neuromuscular research will be presented at the 2026 MDA Clinical ...

Del-desiran reduced DMPK mRNA levels, but led to two serious adverse events ...

MDA Ambassadors: Justin living with limb-girdle muscular dystrophy (LGMD) 2B, Caroline living with collagen VI muscular dystrophy, A.J. living with inclusion body myositis (IBM) and ...